Found 5 matching trials
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
N/ATo obtain short-term and long-term clinical safety information, in pediatri...
Location
Children's National Hospital
Orphan Europe Carbaglu® Surveillance Protocol
N/AThe purpose of this study is to conduct post-marketing surveillance of carg...
Location
Children's National Medical Center
Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia
PHASE3A Phase IIIb (Three b), Randomized Multicentre Comparative Trial to Evaluat...
Location
King Abdullah Specialist Children Hospital, King Abdulaziz Medical City
Long-term Efficacy of Carglumic Acid in Organic Acidemia.
NAEvaluate the Long Term Effectiveness \& Safety of the use of Carglumic Acid...
Location
National Taiwan University Hospital
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
N/AThis is a prospective mixed-design study focused on the long-term managemen...
Location
Hopital Des Enfants, CHU de Bordeaux-GH Pellegrin